| CUSTOMER-1 |
CUSTOMER-1 |
90%
|
For the Three Months Ended March 31, 2026 2025 Product revenues, net Customer 1 39 % 19 % |
| CUSTOMER-2 |
CUSTOMER-2 |
90%
|
For the Three Months Ended March 31, 2026 2025 Product revenues, net Customer 2 20 % 12 % |
| ALNY |
Alnylam Pharmaceuticals, Inc. |
72%
|
exceed revenues historically generated from sales through our EAP, especially in light of current geopolitical issues. Reimbursement of aforementioned products through our EAPs may cease to be availa… |
| ALNY |
Alnylam Pharmaceuticals, Inc. |
72%
|
Reciprocal relationship from ALNY graph: Reciprocal relationship from SRPT graph: exceed revenues historically generated from sales through our EAP, especially in light of current geopolitical issues… |
| ARWR |
Arrowhead Pharmaceuticals, Inc. |
72%
|
Reciprocal relationship from ARWR graph: Reciprocal relationship from SRPT graph: Reciprocal relationship from ARWR graph: Reciprocal relationship from SRPT graph: Reciprocal relationship from ARWR g… |
| ARWR |
Arrowhead Pharmaceuticals, Inc. |
72%
|
past several years to further enhance our internal research and development capabilities. However, we currently do not have internal GMP manufacturing capabilities to produce our products and product… |
| BMRN |
BioMarin Pharmaceutical Inc. |
72%
|
Reciprocal relationship from BMRN graph: Reciprocal relationship from SRPT graph: past several years to further enhance our internal research and development capabilities. However, we currently do no… |
| BMRN |
BioMarin Pharmaceutical Inc. |
72%
|
past several years to further enhance our internal research and development capabilities. However, we currently do not have internal GMP manufacturing capabilities to produce our products and product… |
| CAPR |
Capricor Therapeutics, Inc. |
72%
|
Reciprocal relationship from CAPR graph: be engaged in other clinical trial programs for the same indication as our product candidates or may otherwise be resource constrained. We may be required to … |
| CPRX |
Catalyst Pharmaceuticals, Inc. |
72%
|
Reciprocal relationship from CPRX graph: Reciprocal relationship from SRPT graph: exceed revenues historically generated from sales through our EAP, especially in light of current geopolitical issues… |
| CPRX |
Catalyst Pharmaceuticals, Inc. |
72%
|
exceed revenues historically generated from sales through our EAP, especially in light of current geopolitical issues. Reimbursement of aforementioned products through our EAPs may cease to be availa… |
| IONS |
Ionis Pharmaceuticals, Inc. |
72%
|
exceed revenues historically generated from sales through our EAP, especially in light of current geopolitical issues. Reimbursement of aforementioned products through our EAPs may cease to be availa… |
| IONS |
Ionis Pharmaceuticals, Inc. |
72%
|
Reciprocal relationship from IONS graph: Reciprocal relationship from SRPT graph: exceed revenues historically generated from sales through our EAP, especially in light of current geopolitical issues… |
| KROS |
Keros Therapeutics, Inc. |
72%
|
Reciprocal relationship from KROS graph: nued regulatory review, which may result in significant additional expense and we may be subject to penalties if we fail to comply with regulatory requirement… |
| RGNX |
REGENXBIO Inc. |
72%
|
Reciprocal relationship from RGNX graph: atent that will expire in 2034, one issued U.S. patent that will expire in 2038, one issued U.S. patent that will expire in 2039, one issued U.S. patent that … |
| SNYNF |
Sanofi |
72%
|
Reciprocal relationship from SNYNF graph: Reciprocal relationship from SRPT graph: Reciprocal relationship from SNYNF graph: Reciprocal relationship from SRPT graph: Reciprocal relationship from SNYN… |
| SNYNF |
Sanofi |
72%
|
exceed revenues historically generated from sales through our EAP, especially in light of current geopolitical issues. Reimbursement of aforementioned products through our EAPs may cease to be availa… |
| TRDA |
Entrada Therapeutics, Inc. |
72%
|
Reciprocal relationship from TRDA graph: Reciprocal relationship from SRPT graph: Reciprocal relationship from TRDA graph: everal risks, including disruptions in supply, price increases or late deliv… |
| ANNUAL-REPORT-F-HOFFMAN-LA-ROCHE-LTD |
ANNUAL-REPORT-F-HOFFMAN-LA-ROCHE-LTD |
62%
|
rease overall capacity as well as further reduce risks associated with relying on a limited number of suppliers for manufacturing. Our gene therapy manufacturing capabilities have been greatly enhanc… |
| ARROWHEAD-COLLABORATION-AGREEMENT-SAREPTA-THERAP |
ARROWHEAD-COLLABORATION-AGREEMENT-SAREPTA-THERAP |
62%
|
and certain legal actions in Europe (the “Actions”) would be stopped or withdrawn as between the Settlement Parties. Specifically, the terms of the Settlement Agreement required that existing efforts… |
| BIIB |
Biogen Inc. |
62%
|
Reciprocal relationship from BIIB graph: Reciprocal relationship from SRPT graph: Reciprocal relationship from BIIB graph: Reciprocal relationship from SRPT graph: exceed revenues historically genera… |
| CATALENT-MARYLAND-INC |
CATALENT-MARYLAND-INC |
62%
|
and certain legal actions in Europe (the “Actions”) would be stopped or withdrawn as between the Settlement Parties. Specifically, the terms of the Settlement Agreement required that existing efforts… |
| DELAWARE-GENERAL-CORPORATION |
DELAWARE-GENERAL-CORPORATION |
62%
|
launches and market acceptance of products launched; • changes in the amounts spent to research, develop, acquire, license or promote new and existing products; • results of clinical trial programs; … |
| DOJ-HHS-FALSE-CLAIMS-ACT-WORKING-GROUP |
DOJ-HHS-FALSE-CLAIMS-ACT-WORKING-GROUP |
62%
|
n addition, before we can begin to commercially manufacture and test our product candidates in third-party or our own facilities, we must obtain regulatory approval from the FDA, which includes a rev… |
| F-HOFFMAN-LA-ROCHE-LTD |
F-HOFFMAN-LA-ROCHE-LTD |
62%
|
rease overall capacity as well as further reduce risks associated with relying on a limited number of suppliers for manufacturing. Our gene therapy manufacturing capabilities have been greatly enhanc… |
| MYONEXUS-THERAPEUTICS-INC |
MYONEXUS-THERAPEUTICS-INC |
62%
|
rease overall capacity as well as further reduce risks associated with relying on a limited number of suppliers for manufacturing. Our gene therapy manufacturing capabilities have been greatly enhanc… |
| NATIONWIDE-ARROWHEAD-PHARMACEUTICALS-INC |
NATIONWIDE-ARROWHEAD-PHARMACEUTICALS-INC |
62%
|
and certain legal actions in Europe (the “Actions”) would be stopped or withdrawn as between the Settlement Parties. Specifically, the terms of the Settlement Agreement required that existing efforts… |
| NIPPON-SHINYAKU-CO-LTD |
NIPPON-SHINYAKU-CO-LTD |
62%
|
Patent asserted by Regenx. Plaintiffs seek injunctive relief, a judgment of infringement and willful infringement, damages that are no less than a reasonable royalty (including treble damages), attor… |
| NS-PHARMA-INC |
NS-PHARMA-INC |
62%
|
Patent asserted by Regenx. Plaintiffs seek injunctive relief, a judgment of infringement and willful infringement, damages that are no less than a reasonable royalty (including treble damages), attor… |
| ONO-PHARMACEUTICALS-IONIS-PHARMACEUTICALS-INC |
ONO-PHARMACEUTICALS-IONIS-PHARMACEUTICALS-INC |
62%
|
exceed revenues historically generated from sales through our EAP, especially in light of current geopolitical issues. Reimbursement of aforementioned products through our EAPs may cease to be availa… |